Educational Content: This article is for informational purposes only and does not constitute medical advice. Always consult a healthcare provider for diagnosis and treatment.

Definition of Human gene therapy

Medically reviewed by Dr. Otari Nergadze, Neurosurgeon | Updated: January 2026

Human gene therapy: Insertion of normal DNA directly into cells to correct a genetic defect. The treatment of disease by replacing, altering, or supplementing a gene that is absent or abnormal and whose absence or abnormality is responsible for a disease. 

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